A unique event bringing together leading researchers, patient advocates, and care experts.

Explore the latest breakthroughs in gene therapies and gain insights into effective transitional care strategies. This event promises to ignite discussions, foster collaborations, and inspire a shared commitment to enhancing the lives of those affected by rare disease.

Location: Virtually or at WashU Institute of Public Health Building Taylor Avenue Building (TAB)

• Panel 1: Emerging Gene Therapies for Rare Disease
  Join experts as they discuss groundbreaking treatments, from CRISPR to personalized gene therapies, and their profound impact on rare disease management and the transformative impact these advancements are having on patients’ lives.
• Panel 2: Bridging Care: From Pediatrics to Adulthood
  Patient advocates and experts discuss vital strategies for ensuring consistent care, emotional well-being, and practical solutions to empower patients to thrive as they navigate this pivotal life juncture.